Chief Executive Officer and President
Ultragenyx
Novato, California
Dr. Kakkis is best known for his work developing novel treatments for rare diseases and working on policy issues affecting rare and ultarare disease treatment. Emil is Chief Executive Officer, President and Founder of Ultragenyx, a company with four approved therapies for five rare diseases and multiple late-stage clinical programs. Dr. Kakkis has received numerous awards including the Life Science Leadership Pantheon award from California Life Sciences, a Lifetime Achievement Award from the National MPS Society, the Roscoe O Brady Award for innovation from the WORLD Symposium and the Henri Termeer Visionary Leader Award from BIO, the biotechnology industry organization.
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Keynote: Using Biomarkers to Accelerate Development of Disease Modifying Therapies for Rare Disease
Tuesday, May 14, 2024
1:00 PM – 2:00 PM PT
Hot Topic: Biomarkers and Accelerated Approval for Advanced Therapy
Tuesday, May 14, 2024
2:30 PM – 3:30 PM PT